Sickle Cell Care Reaches an Inflection Point as Gene Therapy Enthusiasm Rises, but Referral Pathways and Uptake Lag Amid Due to Treatment Burden

AI Briefing

• – Gene therapy for sickle cell disease gains traction, but physicians face barriers to widespread adoption
• – Physicians view most patients as suitable for gene therapy, but few have initiated treatment
• – Treatment burden and complex referral pathways hinder gene therapy adoption